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Amicus Therapeutics Announces Presentation and Posters at the SSIEM Annual Symposium 2023

Amicus Therapeutics Announces Presentation and Posters at the SSIEM Annual Symposium 2023

PHILADELPHIA, Aug. 29, 2023 (GLOBE NEWSWIRE) -- (Nasdaq: FOLD), today announced that one oral presentation and five posters across its development programs will be included at the , being held August 29 – September 1, 2023 in Jerusalem, Israel.

Oral Presentation:

Pompe Disease:

Abstract Title: Switching treatment from alglucosidase alfa to cipaglucosidase alfa plus miglustat positively affects motor function and quality of life in patients with late-onset Pompe disease

  • Presenter: Priya Kishnani, MD, MBBS, Duke University Medical Center, Durham, NC, U.S.A.
  • Session: Clinical Studies & Outcomes I
  • Date and time: Wednesday, August 30, 8:45-9:00 a.m. I.D.T.
  • Location: Oren 2

Poster Sessions:

Fabry Disease:

Abstract Title: Multiorgan involvement in females with Fabry disease: results from two phase III trials and the followME registry (Poster #B169)

  • Presenter: Peter Nordbeck, MD, University Hospital Würzburg, Würzburg, Germany
  • Location: Exhibit Hall

Abstract Title: Exploring the Experiences of Females Living with Fabry Disease in Canada (Poster #B12)

  • Presenter: Julia Alton, Executive Director, Canadian Fabry Association, Ontario, Canada
  • Location: Exhibit Hall

Pompe Disease:

Abstract Title: 104-week efficacy and safety of cipaglucosidase alfa plus miglustat in patients with late-onset Pompe disease previously treated with alglucosidase alfa (Poster #B167)

  • Presenter: Tahseen Mozaffar, MD, Department of Neurology, University of California, Irvine, CA, U.S.A.
  • Location: Exhibit Hall

Abstract Title: Safety of home administration of cipaglucosidase alfa plus miglustat in late-onset Pompe disease: results from multiple clinical trials (Poster #B20)

  • Presenter: Ozlem Goker-Alpan, MD, Lysosomal and Rare Disorders Research and Treatment Center, Fairfax, VA, U.S.A
  • Location: Exhibit Hall

Abstract Title: Effect size analysis of cipaglucosidase alfa plus miglustat versus alglucosidase alfa in ERT-experienced adults with late-onset Pompe disease in PROPEL (Poster #B168)

  • Presenter: Tahseen Mozaffar, MD, Department of Neurology, University of California, Irvine, CA, U.S.A.
  • Location: Exhibit Hall

For more information on the SSIEM Annual Symposium 2023, please visit .

About Amicus Therapeutics

Amicus Therapeutics (Nasdaq: FOLD) is a global, patient-dedicated biotechnology company focused on discovering, developing and delivering novel high-quality medicines for people living with rare diseases. With extraordinary patient focus, Amicus Therapeutics is committed to advancing and expanding a pipeline of cutting-edge, first- or best-in-class medicines for rare diseases. For more information please visit the company’s website at , and follow on and .

CONTACTS:

Investors:

Amicus Therapeutics

Andrew Faughnan

Vice President, Investor Relations

(609) 662-3809

Media:

Amicus Therapeutics

Diana Moore

Head of Global Corporate Communications

(609) 662-5079

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EN
29/08/2023

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