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Amicus Therapeutics Announces Upcoming Presentations at the American Society of Gene & Cell Therapy 24th Annual Meeting

Amicus Therapeutics Announces Upcoming Presentations at the American Society of Gene & Cell Therapy 24th Annual Meeting

PHILADELPHIA, May 05, 2021 (GLOBE NEWSWIRE) -- (Nasdaq: FOLD), today announced the acceptance of two abstracts for presentation at the being held virtually, May 11-14, 2021. Accepted abstracts will highlight preclinical data from the Company’s Fabry and Pompe gene therapy programs, which Amicus is developing with the Gene Therapy Program of the Perelman School of Medicine at the University of Pennsylvania.

Digital Poster Session: Tuesday, May 11, 8:00 - 10:00 a.m. ET

Pompe Disease:

  • Title: Post-Symptomatic Reversal of Muscle Pathology in a Model of Pompe Disease Using Gene Therapy
  • Session title: Metabolic, Storage, Endocrine, Liver and Gastrointestinal Diseases
  • Abstract number: 518
  • Presenter: Ali Ramezani, Ph.D., Senior Research Investigator, Project Lead, Translational Research, Gene Therapy Program, University of Pennsylvania

Fabry Disease:

  • Title: Efficacy of Adeno-Associated Viruses Expressing an Engineered Alpha-Galactosidase A Transgene in a Mouse Model of Fabry Disease
  • Session title: Metabolic, Storage, Endocrine, Liver and Gastrointestinal Diseases
  • Abstract number: 519
  • Presenter: CJ (Chunjuan) Song, Ph.D., DABT, Research Director, Translational Research, Gene Therapy Program, University of Pennsylvania

The posters will be made available on the Amicus following their respective presentations at the meeting.

For more information on the American Society of Gene & Cell Therapy 24th Annual Meeting, please visit .

About Amicus Therapeutics

Amicus Therapeutics (Nasdaq: FOLD) is a global, patient-dedicated biotechnology company focused on discovering, developing and delivering novel high-quality medicines for people living with rare metabolic diseases. With extraordinary patient focus, Amicus Therapeutics is committed to advancing and expanding a robust pipeline of cutting-edge, first- or best-in-class medicines for rare metabolic diseases. For more information please visit the company’s website at , and follow us on  and .

CONTACT:

Investors:

Andrew Faughnan

Sr. Director, Investor Relations



(609) 662-3809

Media:

Diana Moore

Head of Global Corporate Communications



(609) 662-5079

FOLD–G



EN
05/05/2021

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